Methods and compounds to modulate inherited genetic diseases.

CL202601798A1Pending Publication Date: 2026-08-14DESIGN THERAPEUTICS INC
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Patent Information

Application Number
CL202601798
Authority / Receiving Office
CL · CL
Patent Type
Applications
Current Assignee / Owner
Priority Date
2024-12-05
Filing Date
2026-06-01
Publication Date
2026-08-14
Patent Text Reader

Abstract

This disclosure relates to transcription modulator compounds, compositions, and methods for the treatment of DM1 (myotonic dystrophy type 1) and FECD (Fuchs corneal endothelial dystrophy).
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