LYSOSOMAL TARGETING OF ENZYMES AND ASSOCIATED USES
MA40791AUndetermined Publication Date: 2017-09-27SHIRE HUMAN GENETIC THERAPIES INC
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Patent Information
- Application Number
- MA40791
- Authority / Receiving Office
- MA · MA
- Patent Type
- Applications
- Current Assignee / Owner
- Priority Date
- 2014-10-24
- Filing Date
- 2015-10-23
- Publication Date
- 2017-09-27
Abstract
The invention provides compositions and methods for efficient lysosomal targeting mediated by pcsk9. In particular, the compositions and methods provided by the invention can be used to treat lysosomal storage diseases such as Pompe disease and Sanfilippo syndrome type b, and they can be used to target lysosomal enzymes to different muscles in the human body.
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