Indole derivatives for targeting autophagy
Patent Information
- Application Number
- NZ834882
- Authority / Receiving Office
- NZ · NZ
- Patent Type
- Applications
- Current Assignee / Owner
- Priority Date
- 2024-01-24
- Filing Date
- 2025-01-23
- Publication Date
- 2025-07-31
AI Technical Summary
Current therapies for modulating autophagy, particularly targeting p62, are limited in their ability to induce selective degradation of pathogenic proteins, and existing technologies like PROTACs face challenges in forming substrate-PROTAC-E3 ligase complexes, restricting their application to a limited set of targets and E3 ligases.
Development of novel heterobifunctional compounds that engage the autophagy adaptor protein p62/SQSTM1, triggering its activation and subsequent assembly of autophagosomes, comprising a targeting ligand and a p62 activating moiety connected by a flexible linker, to enhance the sequestration of targeted proteins within nascent autophagosomes.
This approach allows for precise orchestration of p62 oligomerization and spatial localization, harnessing the cell's autophagic machinery to therapeutically degrade specific targets, including proteins, protein aggregates, and pathogens, offering a broad-spectrum therapeutic modality for diseases characterized by aberrant protein accumulation or defective protein clearance.