Compositions and methods for TTR gene editing and treating ATTR amyloidosis

TW202633659APending Publication Date: 2026-08-16INTELLIA THERAPEUTICS INC
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Patent Information

Application Number
TW114139835
Authority / Receiving Office
TW · TW
Patent Type
Applications
Current Assignee / Owner
Priority Date
2018-05-15
Filing Date
2018-09-28
Publication Date
2026-08-16

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Abstract

Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
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