Treatment of GM1 gangliosidosis
BD2025023A0Pending Publication Date: 2026-08-16AZAFAROS BV
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Patent Information
- Application Number
- BD2025023
- Authority / Receiving Office
- BD · BD
- Patent Type
- Applications
- Current Assignee / Owner
- Filing Date
- 2025-01-20
- Publication Date
- 2026-08-16
Abstract
The invention relates to a compound of formula (I), (I), for use in treating GM1 gangliosidosis. Specifically, the invention relates to a compound of formula (I) for use in reducing the accumulation of GM1 ganglioside in the brain and / or spinal cord of a subject, increasing neuronal survival in a subject, and / or preventing neuronal degeneration in a subject.
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