Methods for treating scn1a, scn8a, or scn5a protein deficiency
CL202600201A1Pending Publication Date: 2026-08-14STOKE THERAPEUTICS INC
View PDF 0 Cites 0 Cited by
Patent Information
- Application Number
- CL202600201
- Authority / Receiving Office
- CL · CL
- Patent Type
- Applications
- Current Assignee / Owner
- Priority Date
- 2024-07-24
- Filing Date
- 2026-01-22
- Publication Date
- 2026-08-14
Abstract
Methods are provided for treating conditions and diseases characterized by SCN1A, SCN8A, or SCN5A protein deficiency, by targeting alternative splicing events in the SCN1A gene and modulating the level of expression of functional proteins in patients with Dravet syndrome and / or inhibiting aberrant protein expression.
Need to check novelty before this filing date? Find Prior Art