Recombinant aav for the gene therapy of wilson disease
EP4684025A1Pending Publication Date: 2026-01-28SKYLINE THERAPEUTICS LTD
-1 Cites 0 Cited by
Patent Information
- Application Number
- EP2024720732
- Authority / Receiving Office
- EP · EP
- Patent Type
- Applications
- Current Assignee / Owner
- Priority Date
- 2023-03-22
- Filing Date
- 2024-03-21
- Publication Date
- 2026-01-28
Smart Images

Figure PCTCN2024082965-FTAPPB-I100001 
Figure PCTCN2024082965-FTAPPB-I100002 
Figure PCTCN2024082965-FTAPPB-I100003
Abstract
The present invention provides a polynucleotide and recombinant AAV encoding a functional copper‐transporting ATPase. The present invention also provides a method of treating Wilson disease comprising administering the recombinant AAV to a subject in need thereof.
Need to check novelty before this filing date? Find Prior Art