AAV gene therapy for treating nervous system diseases
JP2025524548A5Pending Publication Date: 2026-06-30SINEUGENE THERAPEUTICS CO LTD
Patent Information
- Authority / Receiving Office
- JP · JP
- Patent Type
- Applications
- Current Assignee / Owner
- SINEUGENE THERAPEUTICS CO LTD
- Filing Date
- 2023-06-27
- Publication Date
- 2026-06-30
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Abstract
A recombinant adeno-associated virus (rAAV) expression vector comprising a gene encoding a TRIM72 protein or a variant or functional fragment thereof, wherein the recombinant AAV expression vector comprises a neuron-specific promoter, is provided. A pharmaceutical composition comprising the rAAV expression vector and its use are further provided.
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