Method And Compositions For The Treatment Of Fabry Disease
NZ793215BActive Publication Date: 2026-09-01SANGAMO THERAPEUTICS INC
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Patent Information
- Application Number
- NZ793215
- Authority / Receiving Office
- NZ · NZ
- Patent Type
- Patents
- Current Assignee / Owner
- Priority Date
- 2017-08-31
- Filing Date
- 2017-10-19
- Publication Date
- 2026-09-01
- Estimated Expiration
- 2037-10-19
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Figure 1_ABST
Abstract
The disclosure provides nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic alpha galactosidase A (alpha-Gal A) protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and / or prevention of Fabry disease. Further provided are compositions for expressing at least one alpha-Gal A protein.
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