Acid-Responsive Polymeric Nanoparticles for Endosomal GPCR Delivery

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Solution Overview

Problem

Current methods for modulating endosomal GPCR signaling lack effective delivery mechanisms for hydrophobic modulators to the endosomal lumen, limiting therapeutic options for diseases mediated by these receptors.

Innovation Solution

Development of polymeric nanoparticles with an acid-responsive hydrophobic core and hydrophilic shell, containing hydrophobic modulators of endosomal GPCR signaling, which disassemble in acidic environments to release the modulators within the endosomal lumen, allowing targeted interaction with endocytosed receptors.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If hydrophobic modulators are used to target endosomal GPCRs, then therapeutic efficacy is improved, but delivery to the endosomal lumen is insufficient

Engineering Contradiction:
Improvetherapeutic efficacyVSAvoiddelivery to endosomal lumen
Core Design Contradiction:
ReliabilityVSEase of operation

Solution Approach 1:

The patent uses polymeric nanoparticles as an intermediary delivery vehicle to transport hydrophobic modulators through the aqueous cellular environment and into the endosomal lumen. The nanoparticles have a hydrophobic core that encapsulates the modulator and a hydrophilic shell that enables circulation and cellular uptake, solving the delivery problem while maintaining therapeutic efficacy

Inventive Principle:
Principle #24Intermediary (Mediator)

Solution Approach 2:

The patent employs pH-responsive polymer blocks that change their conformation and solubility properties in response to pH changes. The polymer is hydrophobic at physiological pH for stable encapsulation but becomes hydrophilic in the acidic endosomal environment, triggering nanoparticle disassembly and modulator release at the target site

Inventive Principle:
Principle #35Parameter changes

2Adaptability or versatility

If pH-responsive polymers are used for targeted delivery, then specificity to endosomes is improved, but nanoparticle stability in circulation is compromised

Engineering Contradiction:
Improvespecificity to endosomesVSAvoidnanoparticle stability
Core Design Contradiction:
Adaptability or versatilityVSStability of the object's composition

Solution Approach 1:

The patent creates a nanoparticle with spatially differentiated properties: the core remains hydrophobic and stable at physiological pH for protected transport, while the shell contains pH-responsive blocks that only become hydrophilic in the acidic endosomal environment. This local quality differentiation allows simultaneous stability in circulation and specificity at the target

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The nanoparticle structure is designed to be dynamic rather than static. The pH-responsive polymer blocks can reversibly change their conformation and interaction properties in response to environmental pH changes, allowing the nanoparticle to maintain stability under physiological conditions and undergo controlled disassembly in acidic environments

Inventive Principle:
Principle #15Dynamics

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The nanoparticles enable efficient delivery and interaction of hydrophobic modulators with endosomal GPCRs, providing effective treatment for various diseases mediated by endosomal signaling, including pain and inflammatory disorders, with minimal interference with cellular processes.

Implementation Method 1

an acid-responsive hydrophobic polymer block that forms the core of the nanoparticles, wherein the acid-responsive hydrophobic polymer block comprises tertiary amine functional groups that are protonated in an acidic environment

Methodology Applied
Scientific EffectProtonation:

Implementation Method 2

the copolymer chains disassemble and release the hydrophobic modulator of endosomal GPCR signaling into the endosome

Methodology Applied
Scientific EffectpH-responsive phase transition: Phase Change

Implementation Method 3

the nanoparticles enable efficient delivery and interaction of hydrophobic modulators with endosomal GPCRs

Methodology Applied
Scientific EffectHydrophobic interaction: Hydrophobe

Data Source

PatentEP3870236B1Nanoparticle encapsulation to target g protein-coupled receptors in endosomes
Publication Date: 2023.08.09 ENDOSOME THERAPEUTICS INC
  • EP3870236B1 patent drawingFigure 1A~1B
  • EP3870236B1 patent drawingFigure 1C~1D
  • EP3870236B1 patent drawingFigure 2A

AI summary

The present invention relates to methods for modulating endosomal GPCR signaling. In particular, the present invention relates to use of polymeric nanoparticles for the targeted delivery of hydrophobic modulators of endosomal GPCRs and their use in the treatment of associated diseases and disorder.