Amorphous Solid Dispersion for BRAF Inhibitor Bioavailability

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Solution Overview

Problem

Current formulations of biologically active compounds, such as BRAF inhibitors, face challenges in achieving efficacious and safe delivery due to limitations in bioavailability and stability, particularly for treating BRAF-mediated diseases like metastatic melanoma and thyroid cancers.

Innovation Solution

Development of solid dispersions comprising a substantially amorphous Compound I, molecularly dispersed within a polymer matrix like hydroxypropylmethyl cellulose acetate succinate (HPMCAS), combined with excipients and solubilizing agents, to enhance bioavailability and stability, and administered with CYP inhibitors to improve therapeutic efficacy.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If conventional formulations of BRAF inhibitors are used, then the compound can be administered, but bioavailability and stability are insufficient for effective treatment

Engineering Contradiction:
ImprovebioavailabilityVSAvoidformulation complexity
Core Design Contradiction:
ReliabilityVSDevice complexity

Solution Approach 1:

The patent transforms the crystalline compound into an amorphous form, changing its physical state from ordered to disordered molecular arrangement. This parameter change dramatically improves solubility and bioavailability without requiring complex formulation systems, directly resolving the contradiction between reliability and complexity

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent creates a solid dispersion by combining the amorphous compound with a polymer matrix (such as HPMCAS). This composite material approach enhances both stability and bioavailability through the synergistic interaction between the drug and polymer, achieving reliable delivery without excessive formulation complexity

Inventive Principle:
Principle #40Composite materials

2Stability of the object's composition

If crystalline form of Compound I is used, then the formulation is stable, but solubility and bioavailability are limited

Engineering Contradiction:
Improveformulation stabilityVSAvoidsolubility
Core Design Contradiction:
Stability of the object's compositionVSQuantity of substance

Solution Approach 1:

The patent exploits the phase transition from crystalline to amorphous state. The amorphous form, while less stable in isolation, is stabilized within the polymer matrix, achieving both improved solubility and maintained stability. This phase transition approach directly addresses the contradiction between stability and solubility

Inventive Principle:
Principle #36Phase transitions

Solution Approach 2:

The polymer matrix acts as an intermediary between the compound and the aqueous environment. It stabilizes the amorphous compound while simultaneously enhancing its solubility and bioavailability, resolving the contradiction between formulation stability and drug solubility

Inventive Principle:
Principle #24Intermediary (Mediator)

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The solid dispersion formulation significantly improves the bioavailability and therapeutic effectiveness of Compound I, achieving higher exposure levels and target efficacious concentrations, thereby enhancing treatment outcomes for BRAF-mediated diseases.

Implementation Method 1

solid dispersions comprising a substantially amorphous Compound I, molecularly dispersed within a polymer matrix like hydroxypropylmethyl cellulose acetate succinate (HPMCAS)

Methodology Applied
Scientific EffectMolecular dispersion: Dispersion (of waves)

Data Source

PatentEP3700574B1Formulations of a compound modulating kinases
Publication Date: 2024.08.28 PLEXXIKON INC
  • EP3700574B1 patent drawingFigure 1
  • EP3700574B1 patent drawingFigure 2
  • EP3700574B1 patent drawing

AI summary

Provided are solid dispersions of Compound I having the formula: Compound I, wherein Compound I is substantially amorphous, methods of manufacturing said solid dispersions, and methods of using said solid dispersions.