Dynamic BH3 Profiling for Rapid Toxicity Screening

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Solution Overview

Problem

Current methods for assessing drug toxicity are limited, particularly in pre-clinical toxicity testing, which can be expensive and unreliable, and lack efficient alternatives for detecting toxic agents in non-cancerous cells.

Innovation Solution

Dynamic BH3 profiling is used to determine the toxicity of agents by measuring the apoptotic sensitivity of non-cancerous cells through percent BH3 domain peptide-induced mitochondrial outer membrane permeabilization (MOMP) and delta percent priming, allowing for rapid detection of toxic agents.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If traditional pre-clinical toxicity testing methods are used, then comprehensive safety assessment can be obtained, but the testing process becomes expensive and time-consuming

Engineering Contradiction:
Improvetoxicity assessment reliabilityVSAvoidtesting time
Core Design Contradiction:
ReliabilityVSLoss of time

Solution Approach 1:

The patent applies preliminary action by performing BH3 profiling on non-cancerous cells before conducting full pre-clinical toxicity testing. This initial screening step predicts which agents are likely to be toxic, allowing researchers to prioritize only those agents for extensive testing, thereby reducing overall testing time and costs while maintaining reliability.

Inventive Principle:
Principle #10Preliminary action

Solution Approach 2:

The patent uses cell-based BH3 profiling as a simplified model (copy) of the complex in vivo toxicity testing system. By measuring apoptotic sensitivity in cultured non-cancerous cells as a surrogate for whole-organism toxicity, the method provides a faster, cheaper alternative that correlates with clinical outcomes, reducing the need for extensive animal testing.

Inventive Principle:
Principle #26Copying

2Reliability

If traditional pre-clinical toxicity testing methods are used, then comprehensive safety assessment can be obtained, but the cost of testing increases

Engineering Contradiction:
Improvetoxicity assessment reliabilityVSAvoidtesting cost
Core Design Contradiction:
ReliabilityVSLoss of energy

Solution Approach 1:

The patent applies preliminary action by performing BH3 profiling on non-cancerous cells before conducting full pre-clinical toxicity testing. This initial screening step predicts which agents are likely to be toxic, allowing researchers to prioritize only those agents for extensive testing, thereby reducing overall testing time and costs while maintaining reliability.

Inventive Principle:
Principle #10Preliminary action

Solution Approach 2:

The patent uses cell-based BH3 profiling as a simplified model (copy) of the complex in vivo toxicity testing system. By measuring apoptotic sensitivity in cultured non-cancerous cells as a surrogate for whole-organism toxicity, the method provides a faster, cheaper alternative that correlates with clinical outcomes, reducing the need for extensive animal testing.

Inventive Principle:
Principle #26Copying

3Productivity

If dynamic BH3 profiling is used to screen agents, then rapid toxicity detection is achieved, but the method requires new technical procedures

Engineering Contradiction:
Improvetoxicity screening speedVSAvoidmethod complexity
Core Design Contradiction:
ProductivityVSDevice complexity

Solution Approach 1:

The patent applies the taking out principle by extracting and measuring a specific molecular event (BH3 domain peptide-induced MOMP) as a standalone readout for toxicity. By focusing on this single apoptotic initiation event rather than measuring multiple downstream effects, the method simplifies the overall assessment process while maintaining predictive accuracy for clinical toxicity.

Inventive Principle:
Principle #2Taking out (Extraction)

Solution Approach 2:

The patent applies universality by developing a single BH3 profiling methodology that can be applied to screen any agent against any type of non-cancerous cell. This universal approach replaces the need for multiple specialized toxicity assays, simplifying the technical workflow while enabling broad applicability across different drug development programs.

Inventive Principle:
Principle #6Universality (Multi-functionality)

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

This method provides a cost-effective and robust alternative to traditional toxicity testing, enabling the rapid identification of toxic agents and their potential impact on non-cancerous cells, thereby improving the reliability of drug development and safety assessments.

Implementation Method 1

determining a value for percent BH3 domain peptide-induced mitochondrial outer membrane permeabilization (MOMP) in the cells in each of the test aliquots

Methodology Applied
Scientific EffectMitochondrial outer membrane permeabilization (MOMP):

Data Source

PatentEP3289094B1Compositions and methods for assessing toxicity using dynamic BH3 profiling
Publication Date: 2024.06.05 DANA FARBER CANCER INSTITUTE INC
  • EP3289094B1 patent drawingFigure 1A~1D
  • EP3289094B1 patent drawingFigure 1E
  • EP3289094B1 patent drawingFigure 2A~2B

AI summary

The present invention provides methods of assessing toxicity using Dynamic BH3 profiling.