Bile Acid Derivative Salts for Stable FXR Agonist Formulation

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Solution Overview

Problem

Existing bile acid derivatives have low melting points, poor solubility, and stability issues, making them difficult to formulate and store, and they lack effective FXR receptor agonist activity.

Innovation Solution

The development of bile acid derivative salts, specifically hydrochloride and mesylate salts, formed by reacting a compound of Formula (I) with hydrochloric or methanesulfonic acid, enhancing solubility, stability, and FXR receptor agonist activity.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If bile acid derivative compounds are used to treat cholestasis and activate FXR receptor, then therapeutic efficacy is improved, but physical stability and solubility deteriorate due to low melting points and poor solubility

Engineering Contradiction:
Improvetherapeutic efficacyVSAvoidphysical stability
Core Design Contradiction:
ReliabilityVSStability of the object's composition

Solution Approach 1:

The patent applies parameter changes by converting the bile acid derivative from free base form to salt form (hydrochloride or mesylate), which fundamentally changes the physical and chemical parameters of the compound. This transformation increases melting point, improves solubility, and enhances stability while preserving the core therapeutic activity. The salt formation modifies the molecular structure parameters without altering the pharmacophore responsible for FXR receptor activation.

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent creates composite materials by forming salts of bile acid derivatives with specific acids (hydrochloric acid or methanesulfonic acid). This results in a composite structure where the bile acid derivative cation is paired with an anion (chloride or mesylate), creating a new material with combined properties that overcome the limitations of the parent compound while maintaining therapeutic efficacy.

Inventive Principle:
Principle #40Composite materials

2Reliability

If bile acid derivative compounds are used for therapeutic purposes, then FXR receptor agonist activity is achieved, but ease of manufacture and formulation deteriorate due to low melting points and handling difficulties

Engineering Contradiction:
ImproveFXR receptor agonist activityVSAvoidease of formulation
Core Design Contradiction:
ReliabilityVSEase of manufacture

Solution Approach 1:

The patent applies parameter changes by transforming the compound from low-melting-point free base to high-melting-point salt form. This parameter change in melting point (from below 100°C to above 150°C) and solubility characteristics makes the material much easier to handle, weigh, and formulate during manufacturing processes, while preserving the essential FXR agonist activity.

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent uses salt formation as an intermediary step in the manufacturing process. The bile acid derivative is converted to a stable salt form that serves as an intermediate for further formulation development. This intermediary form facilitates easier processing, storage, and formulation while maintaining the ability to achieve the desired therapeutic effect through FXR activation.

Inventive Principle:
Principle #24Intermediary (Mediator)

3Reliability

If bile acid derivative compounds are stored and handled, then therapeutic effects are maintained, but storage stability deteriorates due to poor solubility and handling difficulties

Engineering Contradiction:
Improvetherapeutic effectVSAvoidstorage stability
Core Design Contradiction:
ReliabilityVSDuration of action of stationary object

Solution Approach 1:

The patent applies parameter changes by converting the compound to a salt form with fundamentally different storage characteristics. The hydrochloride and mesylate salts exhibit superior storage stability compared to the free base form, with higher melting points reducing risk of degradation during storage, and improved solubility preventing precipitation and crystallization issues that could compromise stability over time.

Inventive Principle:
Principle #35Parameter changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The salts exhibit improved solubility, stability, and FXR receptor agonist activity, effectively treating cholestasis, reducing portal pressure, and improving liver function, suitable for manufacturing medicaments for chronic liver diseases and metabolic disorders.

Implementation Method 1

a salt of a bile acid derivative, produced by reacting a compound having structure of Formula (F-1) with an acid

Methodology Applied
Scientific EffectIonic bonding: Chemical Bonding

Data Source

PatentEP4053143B1Bile acid derivative salt, crystal structure thereof, preparation method therefor and use thereof
Publication Date: 2026.04.01 XI AN BIOCARE PHARMA LTD
  • EP4053143B1 patent drawingFigure 1~2
  • EP4053143B1 patent drawingFigure 3~4
  • EP4053143B1 patent drawingFigure 5~6

AI summary

The present invention provides a salt of a bile acid derivative, a crystal form thereof, a preparation method therefor and use thereof. The salt of a bile acid derivative, the crystal form thereof and a composition thereof provided by the present invention can improve cholestasis, reduce portal pressure, and improve liver function, and can be used for preparing medicaments for treating or alleviating chronic liver diseases, metabolic diseases, portal hypertension and related diseases.