Screening Compounds Targeting CBP20 and CBP80 for HIV Latency Control

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Solution Overview

Problem

Current treatments for viral infections, particularly HIV, face challenges such as drug resistance, side effects, and the need for long-term administration, with existing therapies failing to cure the infection and allowing viral load rebound due to latent virus reservoirs.

Innovation Solution

A method for screening compounds that interact with or promote the interaction between Cap-Binding Proteins CBP20 and CBP80, specifically targeting the Cap-Binding Complex to inhibit viral replication and reduce viral load, while maintaining minimal cytotoxicity and avoiding resistance development.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If current ART drugs are used to control HIV infection, then viral load is reduced during treatment, but viral load rebounds after treatment discontinuation due to virus latency

Engineering Contradiction:
Improveviral load controlVSAvoidduration of viral suppression
Core Design Contradiction:
ReliabilityVSDuration of action of moving object

Solution Approach 1:

The patent screens compounds that can prevent viral latency establishment in the first place, rather than merely suppressing active replication. By targeting the latent reservoir formation process, the invention aims to eliminate the root cause of rebound before it occurs, enabling potential functional cure strategies.

Inventive Principle:
Principle #10Preliminary action

Solution Approach 2:

The invention uses cellular and molecular markers (such as integration sites, epigenetic markers, and transcriptional intermediates) as mediators to detect and target latent virus reservoirs. These intermediaries provide measurable indicators of latency status, allowing for screening of compounds that can disrupt the latent reservoir maintenance mechanisms.

Inventive Principle:
Principle #24Intermediary (Mediator)

2Reliability

If HAART combination therapy is administered long-term, then disease progression is controlled, but drug resistance and side effects develop

Engineering Contradiction:
Improvedisease controlVSAvoiddrug resistance and side effects
Core Design Contradiction:
ReliabilityVSObject-affected harmful factors

Solution Approach 1:

The patent extracts and targets specific mechanisms unique to viral latency and reservoir maintenance, rather than broadly suppressing all viral replication. By focusing on latency-specific processes (such as integration site selection, epigenetic silencing, and transcriptional repression), the invention seeks to eliminate latent reservoirs without requiring continuous high-dose combination therapy, thereby reducing resistance pressure and side effects.

Inventive Principle:
Principle #2Taking out (Extraction)

Solution Approach 2:

The invention screens compounds that can alter key parameters of latency maintenance, such as chromatin accessibility, transcription factor binding affinity, and integration site distribution. By changing these fundamental parameters that govern latent reservoir persistence, the approach aims to achieve durable control with different mechanisms than current replication inhibitors, potentially overcoming resistance issues.

Inventive Principle:
Principle #35Parameter changes

3Reliability

If indole derivatives are used to interfere with splicing enhancer activity, then viral protein production is suppressed, but cellular toxicity increases

Engineering Contradiction:
Improveviral protein suppressionVSAvoidcellular toxicity
Core Design Contradiction:
ReliabilityVSObject-affected harmful factors

Solution Approach 1:

The patent screens compounds that exhibit selective toxicity toward viral-infected cells or specifically target viral splicing mechanisms while sparing cellular processes. By achieving local specificity in the action mechanism (targeting viral SRSF1 interactions versus cellular splicing factors), the invention aims to maintain antiviral efficacy while reducing off-target cellular damage.

Inventive Principle:
Principle #3Local quality

Data Source

PatentEP3262415B1Methods for screening compounds for treating or preventing a viral infection or a virus-related condition
Publication Date: 2021.05.05 ABIVAX
  • EP3262415B1 patent drawingFigure 1
  • EP3262415B1 patent drawingFigure 2
  • EP3262415B1 patent drawingFigure 3A~3B

AI summary

The present invention relates to a method for screening a compound useful for treating or preventing a viral infection or a virus-related condition in an individual, comprising at least the steps of: a) determining the ability of a candidate compound to promote the interaction between CBP20 and CBP80 in a sample, and b) selecting the candidate compound that is determined to promote said interaction at step a). The present invention further relates to a method for screening a compound useful for treating or preventing a viral infection or virus-related condition in an individual, comprising at least the steps of: a) determining the ability of a candidate compound to interact with CBP20 or CBP80 in a sample, and b) selecting the candidate compound that is determined to interact with CBP20 or CBP80 at step a).