Chimeric Peptide Ganglioside Binding Specificity

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Solution Overview

Problem

Current therapies lack effective solutions for interacting with cell surface gangliosides to treat neurodegenerative disorders, infectious diseases, and cancers, as existing peptides fail to specifically target these sites with high affinity and specificity.

Innovation Solution

A chimeric peptide with a specific amino acid sequence, such as EGVLYVGHHT, is developed, which incorporates histidine residues to bind gangliosides like GM1 and GM3, offering enhanced affinity and specificity, and is modified for proteolytic resistance, allowing it to interact exclusively with gangliosides while ignoring neutral glycolipids.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If existing peptides are used to target gangliosides, then they can potentially interact with cell surface glycolipids, but they fail to achieve high affinity and specificity for gangliosides like GM1 and GM3

Engineering Contradiction:
Improvebinding specificityVSAvoidbinding affinity
Core Design Contradiction:
ReliabilityVSQuantity of substance

Solution Approach 1:

The patent combines the glycolipid-binding domain from α-synuclein (residues 34-45) with the ganglioside-specific motif from Aβ (residues 5-16) to create a chimeric peptide. This merging of functional domains from two different proteins enables the chimeric peptide to achieve both high affinity and specificity for gangliosides GM1 and GM3, resolving the contradiction between binding reliability and binding quantity.

Inventive Principle:
Principle #5Merging (Combining)

Solution Approach 2:

The chimeric peptide functions as a composite molecular structure integrating sequences from two different parental proteins. This composite design allows the peptide to inherit and combine the advantageous binding properties of both parent sequences, achieving enhanced ganglioside recognition that neither parent peptide could achieve alone.

Inventive Principle:
Principle #40Composite materials

2Ease of operation

If the peptide is designed to be short (12-20 amino acids) for ease of administration, then it can cross the blood-brain barrier more effectively, but it may be more susceptible to proteolysis

Engineering Contradiction:
Improveblood-brain barrier penetrationVSAvoidproteolytic resistance
Core Design Contradiction:
Ease of operationVSStability of the object's composition

Solution Approach 1:

The patent applies chemical modifications to the chimeric peptide to alter its physical and chemical parameters, specifically introducing proteolytic resistance while maintaining its short length. These modifications enable the peptide to withstand enzymatic degradation in the bloodstream and brain, resolving the contradiction between ease of operation (BBB penetration) and compositional stability (proteolytic resistance).

Inventive Principle:
Principle #35Parameter changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The chimeric peptide effectively prevents or treats conditions involving gangliosides by binding to GM1 and GM3, reducing neurotoxicity and inhibiting amyloid pore formation, and demonstrates potential in treating neurodegenerative disorders, infectious diseases, and cancers by crossing the blood-brain barrier and interacting with gangliosides with high specificity.

Implementation Method 1

both Aβ and α-synuclein display a common, structurally-related glycolipid-binding domain

Methodology Applied
Scientific EffectGlycolipid binding: Adsorption

Implementation Method 2

The high affinity of Aβ for ganglioside GM1 is determined by the presence of a pair of histidine residues (His-13 and His-14)

Methodology Applied
Scientific EffectElectrostatic interaction: Electrostatics

Implementation Method 3

Kinetics of transendothelial passage of the chimeric peptide α-syn34-45/HH through a monolayer of pure bEnd-3 cells

Methodology Applied
Scientific EffectTransendothelial passage: Permeation

Implementation Method 4

Effect α-syn34-45/HH or α-syn34-45 on amyloid pore formation

Methodology Applied
Scientific EffectInhibition of amyloid formation:

Data Source

PatentEP3116893B1A chimeric peptide that interacts with cell membrane gangliosides
Publication Date: 2019.08.28 FANTINI
  • EP3116893B1 patent drawingFigure 1A
  • EP3116893B1 patent drawingFigure 1B~1C
  • EP3116893B1 patent drawingFigure 2A~2D

AI summary

The invention relates to a chimeric peptide displaying the ganglioside-binding properties of both α-synuclein and β-amyloid peptide. Such peptide is useful in preventing or treating any condition which involves gangliosides as cell surface receptor sites, including neurodegenerative disorders, infectious diseases, or tumors.