Crystalline Piperazine Carboxylate Forms for Stable Bioavailable Dosage

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Solution Overview

Problem

The discovery and selection of solid forms of pharmaceutical compounds are complex and unpredictable, affecting properties such as solubility, stability, and bioavailability, which can lead to formulation issues and market withdrawal, as seen in the case of Ritonavir ™.

Innovation Solution

Development of novel crystalline forms of (R)-5-carbamoylpyridin-3-yl-2-methyl-4-(3-(trifluoromethoxy)benzyl)piperazine-1-carboxylate for oral, mucosal, parenteral, sublingual, transdermal, buccal, or topical administration, characterized by specific X-ray powder diffraction patterns and thermal analysis.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If polymorphic forms of a compound are used, then solubility and bioavailability can be improved, but stability and predictability worsen due to the complex and unpredictable nature of solid form selection

Engineering Contradiction:
ImprovebioavailabilityVSAvoidsolid form selection complexity
Core Design Contradiction:
ReliabilityVSDevice complexity

Solution Approach 1:

The patent performs preliminary identification and characterization of multiple polymorphic forms (Forms I, II, III, IV, V, and VI) with specific XRPD patterns, DSC profiles, and solubility data before product development. This advance knowledge allows selection of the most suitable crystalline form for the intended application, avoiding later formulation failures.

Inventive Principle:
Principle #10Preliminary action

Solution Approach 2:

The patent systematically varies crystallization parameters including solvent type (acetone, ethanol, isopropanol, toluene, dichloromethane), temperature conditions, and pH levels to generate and characterize multiple polymorphic forms. This methodical parameter exploration enables identification of stable forms with optimized bioavailability characteristics.

Inventive Principle:
Principle #35Parameter changes

2Adaptability or versatility

If different crystal forms are discovered, then formulation flexibility and therapeutic benefits are enhanced, but manufacturing and storage stability may deteriorate

Engineering Contradiction:
Improveformulation flexibilityVSAvoidmanufacturing stability
Core Design Contradiction:
Adaptability or versatilityVSStability of the object's composition

Solution Approach 1:

The patent assigns different polymorphic forms to different formulation needs and routes of administration. For example, certain crystalline forms may be selected for oral dosage forms requiring high solubility, while other stable forms are chosen for parenteral preparations requiring storage stability. Each form's properties are optimized for its specific application context.

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The patent conducts comprehensive stability testing and characterization of each polymorphic form under various manufacturing and storage conditions before product development. This includes assessing moisture sensitivity, thermal stability, and chemical stability to anticipate and prevent potential stability issues during later production and storage phases.

Inventive Principle:
Principle #11Beforehand cushioning (Prior cushioning)

3Reliability

If amorphous solids are selected for enhanced dissolution profile, then bioavailability improves, but physical and chemical stability deteriorates

Engineering Contradiction:
Improvedissolution profileVSAvoidphysical stability
Core Design Contradiction:
ReliabilityVSStability of the object's composition

Solution Approach 1:

The patent employs solvatomorph formation by incorporating solvent molecules (acetone, ethanol, isopropanol, toluene, dichloromethane) into the crystal lattice. This approach modifies the dissolution profile through solvent-solute interactions while maintaining the physical stability provided by the crystalline structure, achieving a balance between the benefits of amorphous forms and the stability of crystalline forms.

Inventive Principle:
Principle #35Parameter changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The crystalline forms provide stable and bioavailable dosage forms for treating disorders like pain, neurological disorders, and cancer, enhancing formulation and therapeutic benefits.

Implementation Method 1

crystalline form A having an X-ray powder diffraction pattern comprising peaks at 18.1, 20.1, and 22.3 degrees 2θ ± 0.2 degrees 2θ using Cu Ka radiation at 1.54 Å

Methodology Applied
Scientific EffectX-ray diffraction: X-Ray

Implementation Method 2

characterized by specific X-ray powder diffraction patterns

Methodology Applied
Scientific EffectDiffraction: Diffraction

Implementation Method 3

characterized by specific X-ray powder diffraction patterns and thermal analysis

Methodology Applied
Scientific EffectThermal analysis: Calorimetry

Data Source

PatentEP4434583B1Crystalline (r)-5-carbamoylpyridin-3-yl-2-methyl-4-(3-(trifluoromethoxy)benzyl) piperazine-1-carboxylate, compositions and methods of use thereof
Publication Date: 2026.04.01 CELGENE CORP
  • EP4434583B1 patent drawingFigure 1
  • EP4434583B1 patent drawingFigure 2
  • EP4434583B1 patent drawingFigure 3

AI summary

Provided herein are dosage forms comprising the crystalline forms of (R)-5-carbamoylpyridin-3-yl-2-methyl-4-(3-(trifluoromethoxy)benzyl)piperazine-1-carboxylate and their use in methods of treating diseases and disorders, including inflammatory bowel disease, neurological disorder, or cancer, wherein the method comprises administering the dosage forms to a patient in need thereof.