Engineered Monoacylglycerol Lipase for Detergent-Free Crystallization

Resolve Bottlenecks,
Find Innovative Solutions
Generate Solutions

Solution Overview

Problem

The challenge lies in obtaining well-ordered protein crystals of monoacylglycerol lipase (MGLL) suitable for high-resolution X-ray crystallography, as detergent-solubilized MGLL is prone to aggregation and difficult to crystallize, hindering the discovery of selective inhibitors and structure-based drug design.

Innovation Solution

Engineered forms of MGLL with selective point mutations in the cap-domain, such as mutating hydrophobic residues like Leucine to Serine, Glutamine, or Arginine, and surface lysine residues to Alanine, which do not require detergents for purification, allowing for stable monomeric behavior and improved crystallization, enabling atomic resolution structure determination.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Quantity of substance

If detergent-solubilized MGLL is used for purification, then the protein can be solubilized and purified, but it becomes prone to aggregation and difficult to crystallize

Engineering Contradiction:
Improvesolubility of MGLLVSAvoidcrystallization capability of MGLL
Core Design Contradiction:
Quantity of substanceVSReliability

Solution Approach 1:

The patent applies parameter changes by mutating specific amino acid residues in the cap-domain of MGLL (such as hydrophobic residues like Leucine to Serine, Glutamine, or Arginine, and surface lysine residues to Alanine). These mutations alter the physical and chemical parameters of the protein, specifically reducing hydrophobicity and improving solubility, thereby enabling the protein to be purified without detergents and to form well-ordered crystals suitable for high-resolution X-ray crystallography

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent applies local quality by making selective point mutations only in the cap-domain region of MGLL, rather than throughout the entire protein. This localized modification approach allows the protein to maintain its overall structure and function while improving specific properties (solubility and crystallization capability) in the problematic cap-domain region

Inventive Principle:
Principle #3Local quality

2Quantity of substance

If hydrophobic residues in cap-domain are mutated to polar residues, then solubility improves and detergent requirement is eliminated, but protein structure may be altered

Engineering Contradiction:
Improvesolubility of MGLLVSAvoidstructural integrity of MGLL
Core Design Contradiction:
Quantity of substanceVSStability of the object's composition

Solution Approach 1:

The patent carefully selects amino acid substitutions that change local polarity parameters while preserving overall protein stability. By replacing hydrophobic residues with polar residues (Serine, Glutamine, Arginine) and surface lysine residues with Alanine in the cap-domain, the protein achieves improved solubility and detergent-free purification while maintaining structural integrity suitable for crystallization

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The mutations are localized to the cap-domain, allowing the rest of the protein structure to remain unchanged and maintain its native conformation. This localized modification ensures that the catalytic domain and other functional regions retain their structural integrity while the cap-domain gains improved solubility properties

Inventive Principle:
Principle #3Local quality

3Manufacturing precision

If point mutations are introduced to improve crystallization, then crystal quality improves, but the process complexity increases

Engineering Contradiction:
Improvecrystal order and resolutionVSAvoidprotein engineering complexity
Core Design Contradiction:
Manufacturing precisionVSDevice complexity

Solution Approach 1:

The patent employs selective point mutations focused specifically on the cap-domain region, which contains hydrophobic residues and surface lysine residues known to affect crystallization. By limiting mutations to this specific region rather than the entire protein, the engineering complexity is managed while achieving significant improvements in crystal quality and order

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The patent systematically alters specific amino acid parameters (hydrophobicity, surface charge) in the cap-domain to optimize crystallization properties. These targeted parameter changes produce well-ordered crystals suitable for high-resolution X-ray crystallography without requiring extensive protein engineering throughout the entire protein structure

Inventive Principle:
Principle #35Parameter changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

These engineered forms facilitate the identification of MGLL inhibitors through high-throughput screening and provide a crystal structure suitable for structure-based drug design, enhancing the understanding of MGLL's mechanism and potential therapeutic targeting.

Implementation Method 1

The X-ray diffraction patterns of the crystals of the present invention are of sufficient resolution so that the three-dimensional structure of MGLL can be determined at atomic resolution

Methodology Applied
Scientific EffectX-ray diffraction: X-Ray

Implementation Method 2

The X-ray diffraction patterns of the crystals of the present invention are of sufficient resolution so that the three-dimensional structure of MGLL can be determined

Methodology Applied
Scientific EffectDiffraction: Diffraction

Data Source

PatentEP2180048B1Alternative crystal form of monoacylglycerol lipase (MGLL)
Publication Date: 2014.12.17 JANSSEN PHARMA NV
  • EP2180048B1 patent drawingFigure 1A~1C
  • EP2180048B1 patent drawingFigure 1C
  • EP2180048B1 patent drawingFigure 2A~2C

AI summary

A number of soluble engineered forms of MGLL that are suitable for high-throughput screening and protein crystallization, as well as a crystallized forms of monoacylglycerol lipase protein (MGLL) and descriptions of the X-ray diffraction patterns are disclosed. The engineered constructs of MGLL permit the expression and purification of protein suitable for crystallography or high-throughput screening and identification of ligands, which can function as active agents to MGLL. The X-ray diffraction patterns allow the three dimensional structure of MGLL to be determined at atomic resolution so that ligand binding sites on MGLL can be identified and the interactions of ligands with MGLL amino acid residues can be modeled. Models prepared using such maps permit the design of ligands which can function as active agents which include, but are not limited to, those that function as inhibitors of MGLL.