HGF Beta Chain Mutants Modulate c-Met Signaling

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Solution Overview

Problem

The complexity of the HGF/Met signaling pathway, particularly in understanding HGF-HGF and HGF/Met interactions, has hindered the development of effective therapeutic means, necessitating a better comprehension of the mechanism of action to modulate this pathway effectively.

Innovation Solution

Designing HGF mutants with specific mutations in the β chain's N-terminal region and dimerization domain that impair signaling through the HGF/Met pathway, allowing for the creation of HGF/C-Met antagonist molecules that can inhibit wild-type HGF/HGF and HGF/c-Met interactions, thereby modulating biological functions.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Adaptability or versatility

If HGF mutants with specific mutations in the β chain's N-terminal region and dimerization domain are designed to impair signaling through the HGF/Met pathway, then the ability to modulate biological functions is improved, but the complexity of understanding HGF-HGF and HGF/Met interactions increases

Engineering Contradiction:
Improveability to modulate biological functionsVSAvoidcomplexity of HGF/Met signaling pathway
Core Design Contradiction:
Adaptability or versatilityVSDevice complexity

Solution Approach 1:

The HGF molecule is segmented into functional domains (α-chain, β-chain, N-terminal region, dimerization domain) with specific mutations introduced in the β-chain to selectively impair signaling while preserving other functions. This segmentation allows independent manipulation of different functional regions to achieve precise modulation of biological activities.

Inventive Principle:
Principle #1Segmentation

Solution Approach 2:

Specific local mutations are introduced in the β-chain's N-terminal region and dimerization domain to create HGF variants with altered signaling properties. These localized changes affect only specific interactions (HGF-HGF and HGF/c-Met) while preserving overall structural integrity and other functional capabilities.

Inventive Principle:
Principle #3Local quality

2Reliability

If HGF mutants are designed to compete with wild-type HGF for binding to c-Met, then therapeutic potential for conditions requiring reduced HGF/c-Met activity is improved, but the precision of controlling biological function inhibition deteriorates

Engineering Contradiction:
Improvetherapeutic potentialVSAvoidprecision of controlling biological function inhibition
Core Design Contradiction:
ReliabilityVSManufacturing precision

Solution Approach 1:

Specific amino acid substitutions are introduced in the β-chain (e.g., R494E, R502E, R692E, R699E) to alter binding parameters and signaling efficiency. These parameter changes enable precise control over the degree of biological function inhibition, allowing therapeutic modulation rather than complete blockade.

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The HGF mutants are designed to partially inhibit HGF/c-Met interactions rather than completely block them. This partial action provides therapeutic benefit by reducing excessive signaling in pathological conditions while maintaining sufficient activity for essential physiological functions.

Inventive Principle:
Principle #16Partial or excessive action

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

These mutant molecules effectively compete with wild-type HGF for binding to c-Met, reducing biological functions associated with the HGF/c-Met axis, providing therapeutic potential for conditions requiring reduced but not complete inhibition of HGF/c-Met activity.

Implementation Method 1

The protease-like domain of HGF (HGF β-chain) is devoid of catalytic activity since it lacks the required Asp [c102]-His [c57]-Ser [c195] (standard chymotrypsinogen numbering in brackets throughout) catalytic triad found in all serine proteases

Methodology Applied
Scientific EffectProtein-protein binding:

Implementation Method 2

Acquisition of HGF signaling activity is contingent upon proteolytic cleavage (activation) of scHGF at Arg494-Val495 resulting in the formation of mature HGF, a disulfide-linked α/β heterodimer

Methodology Applied
Scientific EffectProteolytic cleavage:

Implementation Method 3

Acquisition of HGF signaling activity is contingent upon proteolytic cleavage (activation) of scHGF at Arg494-Val495 resulting in the formation of mature HGF, a disulfide-linked α/β heterodimer

Methodology Applied
Scientific EffectDisulfide bonding:

Data Source

PatentEP1869070B1HGF beta chain variants
Publication Date: 2013.11.27 GENENTECH INC
  • EP1869070B1 patent drawingFigure 1A
  • EP1869070B1 patent drawingFigure 1B
  • EP1869070B1 patent drawingFigure 1C

AI summary

The invention provides HGF/Met modulators comprising HGF having mutations in regions that affect HGF function, and antagonists that target said regions. The invention further provides methods of identifying, making and using these modulators.