Immortalized Corneal Stem Cell Exosomes for Scar Reduction

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Solution Overview

Problem

The severe shortage of transplantable cornea tissues for treating corneal scarring and the limitations of conventional therapies, including the undefined components of exosomes, hinder effective treatment options for corneal blindness.

Innovation Solution

Development of exosomes derived from immortalized corneal stromal stem cells, which produce a consistent supply of defined polynucleotides and proteins to reduce scarring by delivering therapeutic agents directly to corneal tissues, avoiding the need for surgical intervention.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If corneal transplantation is performed to treat corneal scarring, then vision restoration is achieved, but the severe shortage of transplantable cornea tissues limits availability to less than 5% of affected people

Engineering Contradiction:
Improvevision restoration efficacyVSAvoidavailability of transplantable cornea tissues
Core Design Contradiction:
ReliabilityVSQuantity of substance

Solution Approach 1:

The invention extracts and utilizes specific functional components (exosomes containing polynucleotides and proteins) from corneal stromal stem cells, rather than transplanting entire corneal tissues. This extraction approach enables production of therapeutic agents without requiring scarce donor corneas, thereby resolving the contradiction between treatment efficacy and tissue availability

Inventive Principle:
Principle #2Taking out (Extraction)

Solution Approach 2:

The invention creates copies of therapeutic molecules (polynucleotides and proteins) that are naturally present in corneal stromal stem cell exosomes. By identifying and replicating these specific molecular components, the invention enables mass production of therapeutic agents that mimic the healing effects of natural corneal tissues without requiring actual tissue transplants

Inventive Principle:
Principle #26Copying

2Adaptability or versatility

If conventional exosome therapy is used for corneal scarring, then treatment potential is achieved, but the undefined components of exosomes create challenges in therapy standardization

Engineering Contradiction:
Improvetherapeutic potential of exosomesVSAvoiddefinition of exosome components
Core Design Contradiction:
Adaptability or versatilityVSManufacturing precision

Solution Approach 1:

The invention focuses on specific local components within exosomes (particular polynucleotides and proteins) rather than treating exosomes as undifferentiated entities. By identifying and isolating specific therapeutic molecules with defined sequences and functions, the invention enables precise manufacturing and standardization while retaining the therapeutic versatility of exosome-based therapy

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The invention segments the complex exosome structure into identifiable and isolatable components (specific polynucleotides and proteins). This segmentation allows for separate characterization, purification, and standardization of individual therapeutic molecules, thereby resolving the manufacturing precision challenges while preserving the overall therapeutic adaptability

Inventive Principle:
Principle #1Segmentation

3Reliability

If primary stem cells are used to obtain exosomes, then therapeutic effectiveness is maintained, but the limited availability and lifespan of primary cells restricts scalable production

Engineering Contradiction:
Improvetherapeutic effectiveness of exosomesVSAvoidscalability of exosome production
Core Design Contradiction:
ReliabilityVSProductivity

Solution Approach 1:

The invention identifies and replicates the specific polynucleotide and protein profiles found in primary stem cell-derived exosomes. By copying these molecular signatures through controlled expression systems, the invention enables scalable production of therapeutically equivalent exosomes without being constrained by the limited availability and lifespan of primary stem cells

Inventive Principle:
Principle #26Copying

Data Source

PatentEP3758756B1Stem cell-derived exosomes for the treatment of corneal scarring
Publication Date: 2025.09.03 RGT UNIV OF CALIFORNIA
  • EP3758756B1 patent drawingFigure 1A~1B
  • EP3758756B1 patent drawingFigure 2
  • EP3758756B1 patent drawingFigure 3A~3F

AI summary

Corneal stromal scars are the leading cause of corneal blindness. The present invention relates to methods and compositions useful in therapies for this pathological condition. The invention provides corneal stromal stem cells and certain other stem cells and as well as exosome polynucleotides produced by such cells, and methods for making and using these cells and compositions. The invention is based upon the discovery that exosomes and their associate active components obtained from these cells comprise agents having the same capacity as corneal stromal stem cells to reduce scarring and prevent scar formation in patients having corneal damage.