Plasma Kallikrein Inhibitor Solid Form Stability

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Solution Overview

Problem

Current plasma kallikrein inhibitors, such as Ecallantide, are often large proteins that can cause anaphylactic reactions and have limitations in stability and handling during pharmaceutical manufacturing, and existing small molecule inhibitors may have polar and ionizable functional groups that affect their efficacy and stability.

Innovation Solution

Development of a novel solid form (Form 1) of the compound of Formula A, characterized by specific X-ray powder diffraction peaks, which exhibits improved physico-chemical properties like reduced hygroscopicity, stability, and ease of processing, suitable for oral solid dosage forms.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If large protein plasma kallikrein inhibitors (such as Ecallantide) are used, then therapeutic efficacy is achieved, but anaphylactic reactions occur and manufacturing stability is compromised

Engineering Contradiction:
Improvetherapeutic efficacyVSAvoidanaphylactic reactions
Core Design Contradiction:
ReliabilityVSObject-affected harmful factors

Solution Approach 1:

The patent changes the molecular size parameter by transitioning from large protein inhibitors to small molecule inhibitors, thereby maintaining therapeutic efficacy while eliminating anaphylactic reactions and improving manufacturing stability

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent employs small molecule inhibitors that can be easily synthesized and disposed of, replacing complex protein inhibitors that require sophisticated manufacturing and have stability issues

Inventive Principle:
Principle #27Cheap short-living objects (Disposable)

2Ease of manufacture

If small molecule plasma kallikrein inhibitors are used, then manufacturing stability improves, but polar and ionizable functional groups affect efficacy and stability

Engineering Contradiction:
Improvemanufacturing stabilityVSAvoidtherapeutic efficacy
Core Design Contradiction:
Ease of manufactureVSReliability

Solution Approach 1:

The patent modifies the chemical structure parameters of small molecule inhibitors by removing or modifying polar and ionizable functional groups, thereby maintaining manufacturing stability while preserving therapeutic efficacy

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent extracts or removes problematic polar and ionizable functional groups from the small molecule inhibitor structure, eliminating their negative effects on efficacy and stability while retaining the core inhibitory activity

Inventive Principle:
Principle #2Taking out (Extraction)

3Ease of manufacture

If conventional solid forms of plasma kallikrein inhibitors are used, then dosage form preparation is straightforward, but hygroscopicity and processing difficulty increase

Engineering Contradiction:
Improvedosage form preparationVSAvoidhygroscopicity
Core Design Contradiction:
Ease of manufactureVSObject-affected harmful factors

Solution Approach 1:

The patent changes the physical state parameters by developing a novel solid form with specific crystal structure, thereby reducing hygroscopicity and improving processing ease while maintaining straightforward dosage form preparation

Inventive Principle:
Principle #35Parameter changes

Data Source

PatentEP3716952B1Dosage forms comprising a plasma kallikrein inhibitor
Publication Date: 2022.01.05 KALVISTA PHARMA
  • EP3716952B1 patent drawingFigure 1a
  • EP3716952B1 patent drawingFigure 1b
  • EP3716952B1 patent drawingFigure 1c

AI summary

The present inventionrelates tooral solid dosage forms comprising a plasma kallikrein inhibitor, in particular a solid form (Form 1) of the compoundof Formula A. Also provided are methods of preparing oral solid dosage forms comprising the compound of Formula A using Form 1 of the compound of Formula A.