Mineralocorticoid Receptor Antagonists for Retinal Fluid Reduction

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Solution Overview

Problem

Fluid accumulation in and under the retina, particularly in conditions such as diabetic retinopathy, glaucoma, and age-related macular degeneration, is not effectively managed by current treatments, which often lead to severe side effects due to the molecular mechanisms underlying retinal hydration remaining unexplored.

Innovation Solution

The use of mineralocorticoid receptor (MR) antagonists, including anti-sense oligonucleotides, small interfering RNAs (siRNAs), and ribozymes, to inhibit MR gene expression, which regulates aquaporin and Kir4.1 expression in Müller glial cells, thereby addressing fluid accumulation issues associated with metabolic perturbations and retinal diseases.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Quantity of substance

If traditional glucocorticoid treatments are used to manage fluid accumulation in the retina, then fluid accumulation is reduced, but severe side effects occur

Engineering Contradiction:
Improvefluid accumulationVSAvoidsevere side effects
Core Design Contradiction:
Quantity of substanceVSObject-affected harmful factors

Solution Approach 1:

The patent changes the molecular target parameter from glucocorticoid receptors to mineralocorticoid receptors. By using MR antagonists instead of glucocorticoids, the treatment achieves fluid reduction through a different molecular pathway (modulating aquaporin and Kir4.1 expression) that avoids the severe side effects associated with traditional glucocorticoid therapy.

Inventive Principle:
Principle #35Parameter changes

2Quantity of substance

If current treatments for retinal fluid accumulation are used, then some fluid reduction is achieved, but the molecular mechanisms remain unexplored leading to ineffective management

Engineering Contradiction:
Improvefluid accumulationVSAvoideffective management
Core Design Contradiction:
Quantity of substanceVSReliability

Solution Approach 1:

The patent incorporates feedback by modulating the expression of specific ion channels (Kir4.1) and water channels (aquaporins) in Müller glial cells. This targeted approach allows for precise control of retinal hydration based on the molecular mechanisms underlying fluid accumulation, improving reliability of treatment management.

Inventive Principle:
Principle #23Feedback

3Object-affected harmful factors

If MR antagonists are used to treat retinal fluid accumulation, then fluid accumulation is reduced with fewer side effects, but the treatment targets previously unexplored molecular mechanisms

Engineering Contradiction:
Improveside effectsVSAvoidmolecular mechanism complexity
Core Design Contradiction:
Object-affected harmful factorsVSDevice complexity

Solution Approach 1:

The patent uses MR antagonists as intermediary molecules that block mineralocorticoid receptor activation. This intermediary approach modulates the expression of downstream targets (aquaporins and Kir4.1 channels) without directly interfering with the complex molecular pathways, thereby reducing side effects while managing the underlying molecular complexity.

Inventive Principle:
Principle #24Intermediary (Mediator)

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

This approach effectively reduces fluid accumulation in the retina by modulating ion and water channels, offering a novel treatment for conditions like diabetic retinopathy and age-related macular degeneration while minimizing the severe side effects of traditional glucocorticoid treatments.

Implementation Method 1

Ion channels and aquaporins are differentially expressed in retinal cells, and play important roles in ion and water movements that are crucial for adequate control of retinal hydration

Methodology Applied
Scientific EffectOsmosis: Osmosis

Data Source

PatentEP3238781B1Methods and compositions for the treatment of fluid accumulation in and/ or under the retina
Publication Date: 2019.07.31 ASSISTANCE PUBLIQUE HOPITAUX DE PARIS (APHP)
  • EP3238781B1 patent drawingFigure 1~2
  • EP3238781B1 patent drawingFigure 3
  • EP3238781B1 patent drawingFigure 4

AI summary

The present invention provides methods and compositions for the treatment of fluid accumulation in and/or under the retina.