Peptide C-Terminal Modification for VEGFR-1 Inhibition

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Solution Overview

Problem

Existing synthetic peptides for inhibiting VEGFR-1 interactions with VEGF-A and PIGF ligands are not efficient at low concentrations and lack effectiveness when administered orally, limiting their therapeutic potential for angiogenesis-related pathologies.

Innovation Solution

Modifying the C-terminal of a tetrameric peptide with an amino acid having a steric hindrance comparable to a thiol or thioether group, such as R-Glu-S-Cys(Bzl)-S-Cha, enhances the peptide's ability to inhibit VEGFR-1 interactions with VEGF-A and PIGF, achieving a 50% inhibition at concentrations below 1000 nM, and maintains therapeutic efficacy when administered orally.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If the original tetrameric peptide (iVR1) is used, then it can bind VEGFR-1 and inhibit VEGF-A/PIGF interaction, but the inhibitory concentration (IC50) is around 10 μM which is not efficient enough

Engineering Contradiction:
Improveinhibitory capacityVSAvoidconcentration required for 50% inhibition
Core Design Contradiction:
ReliabilityVSQuantity of substance

Solution Approach 1:

The patent modifies the C-terminal of the peptide by introducing a chemical group with steric hindrance (Cys(Bzl) or Cha amino acid residue), which changes the peptide's binding parameters to achieve higher affinity for VEGFR-1, reducing the IC50 from 10 μM to below 1000 nM

Inventive Principle:
Principle #35Parameter changes

2Reliability

If the original peptide is administered orally, then it can inhibit choroidal neovascularization, but the therapeutic efficacy is limited compared to intravitreal administration

Engineering Contradiction:
Improvetherapeutic efficacyVSAvoidadministration route
Core Design Contradiction:
ReliabilityVSEase of operation

Solution Approach 1:

The peptide modification at the C-terminal with steric hindrance groups improves the peptide's pharmacokinetic properties, enabling effective oral bioavailability and maintaining therapeutic efficacy when administered orally, thus eliminating the need for invasive intravitreal injections

Inventive Principle:
Principle #35Parameter changes

3Ease of manufacture

If synthetic compounds are used instead of monoclonal antibodies, then production cost and complexity are reduced, but binding affinity and specificity may be compromised

Engineering Contradiction:
Improveproduction cost and complexityVSAvoidbinding affinity
Core Design Contradiction:
Ease of manufactureVSReliability

Solution Approach 1:

The patent optimizes the peptide sequence and structure (introducing steric hindrance at C-terminal) to achieve binding affinity comparable to monoclonal antibodies while maintaining the advantages of synthetic production - lower cost, simpler manufacturing, and improved stability

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The peptide combines multiple functional features: VEGFR-1 binding capability, steric hindrance for enhanced affinity, and oral bioavailability properties, creating a multi-functional synthetic compound that bridges the gap between simplicity and effectiveness

Inventive Principle:
Principle #40Composite materials

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The modified peptide, iVR1-Cys, demonstrates a 10-fold improvement in inhibitory capacity and achieves significant inhibition of choroidal neovascularization, both intravitreally and orally, compared to the unmodified peptide, iVR1.

Implementation Method 1

capable of binding VEGFR-1 and able to interfere in the interaction between the VEGF-A, PIGF, VEGF-B ligands and VEGF-A/PIGF heterodimer with VEGFR-1

Methodology Applied
Scientific EffectBinding:

Implementation Method 2

capacity to compete, in a dose-dependent manner, with VEGF-A and/or PIGF in binding with VEGFR-1

Methodology Applied
Scientific EffectCompetition:

Implementation Method 3

has shown anti-angiogenic activity in vitro, interfering with the pro-angiogenic activity of PIGF and VEGF-A

Methodology Applied
Scientific EffectAnti-angiogenic activity:

Implementation Method 4

when administered orally, or by gavage, both the peptide described in Ponticelli et al. and the peptides of the present invention have demonstrated a significant capacity to inhibit choroidal neovascularization

Methodology Applied
Scientific EffectInhibition of neovascularization:

Data Source

PatentEP3849582B1Peptides and medical uses thereof
Publication Date: 2025.12.31 ANBITION SRL
  • EP3849582B1 patent drawingFigure 1
  • EP3849582B1 patent drawingFigure 2
  • EP3849582B1 patent drawingFigure 3

AI summary

The present invention relates to peptides, a composition comprising said peptides and the use thereof as inhibitors of angiogenesis and/or neoangiogenesis. Furthermore, the present invention relates to the use of said peptides and said composition for the treatment of pathologies correlated with an incorrect angiogenesis and/or neoangiogenesis. In particular, in this context reference is made to angiogenesis and/or neoangiogenesis correlated with VEGFR1.