SLE Treatment Compound Modulating Autoantibody Production

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Solution Overview

Problem

Current treatments for systemic lupus erythematosus (SLE) often rely on NSAIDs, low-potency immunosuppressants, and corticosteroids, which may not adequately manage the disease, particularly in severe cases, and there is a need for prophylactic or therapeutic drugs that can effectively treat or prevent SLE.

Innovation Solution

Administration of a therapeutically effective amount of Compound I, specifically (S)-3-[4-(4-morpholin-4-ylmethylbenzyloxy)-1-oxo-1,3-dihydro-isoindol-2-yl]piperidine-2,6-dione, or its pharmaceutically acceptable salts, solvates, hydrates, stereoisomers, or racemic mixtures, over a period of 56 days, which targets immune response dysregulation and autoantibody production.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If current standard treatments (NSAIDs, low-potency immunosuppressants, corticosteroids) are used for SLE, then the treatment approach is simple and well-established, but the therapeutic efficacy is insufficient for severe cases and prophylactic needs

Engineering Contradiction:
Improvetherapeutic efficacyVSAvoidtreatment complexity
Core Design Contradiction:
ReliabilityVSDevice complexity

Solution Approach 1:

The patent applies parameter changes by modifying the chemical structure of existing immunosuppressive agents to create Compound I with enhanced therapeutic properties. The specific molecular modifications result in a compound that provides superior therapeutic efficacy for SLE while maintaining manageable treatment protocols, directly resolving the contradiction between efficacy and complexity

Inventive Principle:
Principle #35Parameter changes

2Reliability

If more potent immunosuppression is used to treat severe SLE, then therapeutic efficacy improves, but side effects and treatment risks increase

Engineering Contradiction:
Improvedisease controlVSAvoidside effects
Core Design Contradiction:
ReliabilityVSObject-affected harmful factors

Solution Approach 1:

The patent applies local quality by designing Compound I to selectively target pathological immune responses in SLE while sparing normal physiological functions. The compound demonstrates preferential activity against disease-related immune pathways, achieving effective disease control with reduced impact on healthy tissues, thereby resolving the contradiction between disease control and side effects

Inventive Principle:
Principle #3Local quality

3Reliability

If prophylactic treatment is implemented for SLE, then disease prevention is improved, but the need for long-term medication increases

Engineering Contradiction:
Improvedisease preventionVSAvoidtreatment duration
Core Design Contradiction:
ReliabilityVSDuration of action of moving object

Solution Approach 1:

The patent applies continuity of useful action by developing Compound I with pharmacokinetic properties that maintain sustained therapeutic levels in the body. The compound's prolonged half-life and consistent bioavailability enable effective prophylactic treatment with less frequent dosing, addressing the contradiction between disease prevention and treatment duration by making long-term therapy more practical and manageable

Inventive Principle:
Principle #20Continuity of useful action

Data Source

PatentEP3145513B13-(4-((4-(morpholinomethyl-benzyl)oxy)-1-oxoisoindolin-2-YL)piperidine-2,6-dione for the treatment of systemic lupus erythematosus
Publication Date: 2023.11.15 CELGENE CORP
  • EP3145513B1 patent drawingFigure 1
  • EP3145513B1 patent drawingFigure 2A~2B
  • EP3145513B1 patent drawingFigure 2C

AI summary

Provided herein are methods of using compounds and compositions for treating, managing, and/or preventing systemic lupus erythematosus (SLE). Pharmaceutical compositions and dosing regimens for use in the methods are also provided herein.