Stable Soluble Human TNF Alpha Antibodies

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Solution Overview

Problem

Current anti-TNFα antibodies for treating TNF-mediated disorders, such as rheumatoid arthritis, have limitations in stability, solubility, and immunogenicity, necessitating the development of more effective and stable antibody forms for continuous treatment.

Innovation Solution

Development of stable and soluble antibodies with aggregation-reducing modifications, specifically optimized light chain and heavy chain sequences for scFv antibodies and Fab fragments, which include modifications like arginine substitution at specific positions to enhance stability and reduce immunogenicity, allowing for effective binding to TNFα and treatment of TNFα-mediated disorders.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Stability of the object's composition

If conventional anti-TNFα antibodies are used, then TNFα binding activity is achieved, but stability and solubility are insufficient leading to aggregation

Engineering Contradiction:
Improveantibody stabilityVSAvoidcontinuous treatment capability
Core Design Contradiction:
Stability of the object's compositionVSReliability

Solution Approach 1:

The patent applies parameter changes by modifying amino acid sequences at specific positions (e.g., position 42 in VL domain, position 89 in VH domain) to alter the physical-chemical properties of the antibody. These sequence modifications change the aggregation propensity and stability parameters of the antibody molecule, enabling improved solubility and reduced aggregation while maintaining TNFα binding activity.

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent implements local quality by making targeted amino acid substitutions at specific local positions within the antibody variable domains rather than global modifications. The modifications focus on critical interfaces and regions prone to aggregation (such as the VL-VH interface and CDR regions), leaving other functional regions unchanged to preserve binding activity while improving local stability properties.

Inventive Principle:
Principle #3Local quality

2Quantity of substance

If antibody concentration is increased for continuous treatment, then therapeutic efficacy is improved, but aggregation increases reducing solubility

Engineering Contradiction:
Improveantibody concentrationVSAvoidaggregation tendency
Core Design Contradiction:
Quantity of substanceVSStability of the object's composition

Solution Approach 1:

The patent changes the aggregation parameter of the antibody through amino acid sequence modification, allowing the antibody to maintain stability at higher concentrations. The modified sequences reduce intermolecular aggregation interactions, enabling formulation at higher antibody concentrations necessary for continuous treatment without precipitating or aggregating.

Inventive Principle:
Principle #35Parameter changes

Solution Approach 2:

The patent converts the harmful aggregation tendency into a beneficial property by selecting amino acid substitutions that specifically reduce aggregation propensity. The modifications at positions prone to aggregation (such as hydrophobic patches and interface regions) transform the antibody from an aggregation-prone molecule into a stable, soluble therapeutic suitable for high-concentration formulations.

Inventive Principle:
Principle #22Blessing in disguise (Convert harm into benefit)

3Stability of the object's composition

If antibody modifications are made to reduce aggregation, then stability is improved, but binding affinity to TNFα may be affected

Engineering Contradiction:
ImprovesolubilityVSAvoidbinding specificity
Core Design Contradiction:
Stability of the object's compositionVSManufacturing precision

Solution Approach 1:

The patent carefully selects modification sites that are local to aggregation-prone regions but distinct from the TNFα binding interface. By modifying specific positions in the framework regions and non-critical CDR positions while preserving the antigen-binding CDRs, the patent achieves local improvement in solubility without affecting the global binding function.

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The patent applies partial action by making limited, targeted amino acid substitutions rather than extensive modifications. The modifications are applied selectively at key positions (such as one or two critical residues per variable domain) sufficient to reduce aggregation, avoiding excessive changes that could disrupt binding affinity or alter the antibody's functional properties.

Inventive Principle:
Principle #16Partial or excessive action

Data Source

PatentEP3336105B1Stable and soluble human TNF alpha antibodies
Publication Date: 2020.11.04 NOVARTIS AG
  • EP3336105B1 patent drawingFigure 1
  • EP3336105B1 patent drawingFigure 2A~2B
  • EP3336105B1 patent drawingFigure 3A~3B

AI summary

The invention provides antibodies that are modified to reduce aggregration propensity, and methods of producing such antibodies. The present invention also provides particularly stable and soluble scFv antibodies and Fab fragments specific for TNF, which comprise specific light chain and heavy chain sequences that are optimized for stability, solubility, in vitro and in vivo binding of TNF, and low immunogenicity. The nucleic acids, vectors and host cells for expression of the recombinant antibodies of the invention, methods for isolating them and the use of said antibodies in medicine are also disclosed.