Unstructured Recombinant Polymers Extend Serum Half-Life

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Solution Overview

Problem

Current methods for modifying proteins with polymers, such as PEGylation, face challenges including complex multi-step processes, product mixture separation, and limitations in site-specific attachment, leading to reduced therapeutic activity and immunogenicity concerns, especially with pathogen-derived sequences.

Innovation Solution

The development of unstructured recombinant polymers (URPs) comprising at least 200 contiguous amino acids with a high percentage of glycine, aspartate, alanine, serine, threonine, glutamate, and proline residues, which are designed to minimize non-specific binding and enhance serum stability and solubility, allowing for the creation of multidomain proteins with extended serum half-life and reduced immunogenicity.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Duration of action of stationary object

If chemical conjugation of polymers to proteins is performed, then serum half-life is extended, but the process becomes complex and requires multi-step procedures

Engineering Contradiction:
Improveserum half-lifeVSAvoidprocess complexity
Core Design Contradiction:
Duration of action of stationary objectVSDevice complexity

Solution Approach 1:

The polymer is genetically fused to the protein before expression, eliminating the need for post-purification conjugation steps. The fusion protein is directly expressed and purified in a single step, resolving the contradiction between extending serum half-life and reducing process complexity.

Inventive Principle:
Principle #10Preliminary action

Solution Approach 2:

The polymer and protein are combined into a single genetic construct that is co-expressed as a fusion protein. This merging eliminates separate conjugation steps and simplifies the overall manufacturing process while maintaining the serum half-life extension benefit.

Inventive Principle:
Principle #5Merging (Combining)

2Reliability

If site-specific PEGylation is performed, then therapeutic activity is maintained, but the process requires careful control and has difficulty eliminating side reactions

Engineering Contradiction:
Improvetherapeutic activityVSAvoidprocess control
Core Design Contradiction:
ReliabilityVSEase of manufacture

Solution Approach 1:

The chemical conjugation process is replaced with a genetic fusion approach. Instead of using chemical reagents and controlling complex reaction conditions, the polymer-protein linkage is established through genetic coding, eliminating side reactions and simplifying process control while maintaining therapeutic activity.

Inventive Principle:
Principle #28Mechanics substitution (Replace mechanical system)

3Duration of action of stationary object

If pathogen-derived sequences are used for polymer modification, then serum half-life is extended, but immunogenicity increases

Engineering Contradiction:
Improveserum half-lifeVSAvoidimmunogenicity
Core Design Contradiction:
Duration of action of stationary objectVSObject-generated harmful factors

Solution Approach 1:

The polymer sequence is engineered with specific local characteristics - using repetitive sequences with low information content that mimic host proteins. This local quality modification extends serum half-life while reducing immunogenicity by making the polymer appear more 'self-like' to the immune system.

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The sequence parameters of the polymer are optimized by using repetitive amino acid sequences with specific compositional characteristics. These parameter changes (sequence composition, repetitiveness, low information content) simultaneously extend serum half-life and reduce immunogenicity.

Inventive Principle:
Principle #35Parameter changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

URPs significantly increase the serum half-life and solubility of proteins, reduce immunogenicity, and improve manufacturing and characterization by forming stable, non-aggregating products with enhanced therapeutic properties.

Implementation Method 1

These polymers exert their effect by increasing the hydrodynamic radius (also called Stokes' radius) of the modified protein relative to the unmodified protein, which reduces the rate of clearance by kidney filtration

Methodology Applied
Scientific EffectHydrodynamic radius effect: Stokes Drift

Implementation Method 2

In addition, polymer attachment can reduce interaction of the modified protein with other proteins, cells, or surfaces

Methodology Applied
Scientific EffectSteric hindrance:

Data Source

PatentEP2402754B2Unstructured recombinant polymers and uses thereof
Publication Date: 2023.07.26 AMUNIX PHARMACEUTICALS INC
  • EP2402754B2 patent drawingFigure 1
  • EP2402754B2 patent drawingFigure 2
  • EP2402754B2 patent drawingFigure 3

AI summary

The present invention provides unstructured recombinant polymers (URPs) and proteins containing one or more of the URPs. The present invention also provides microproteins, toxins and other related proteinaceous entities, as well as genetic packages displaying these entities. The present invention also provides recombinant polypeptides including vectors encoding the subject proteinaceous entities, as well as host cells comprising the vectors. The subject compositions have a variety of utilities including a range of pharmaceutical applications.