Zinc Finger Linkers for Gap-Specific DNA Binding

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Solution Overview

Problem

Current linkers for zinc-finger proteins fail to selectively bind targets with 1, 2, or 3 base pair gaps, lacking the necessary affinity and specificity, which limits their design capability and effectiveness in gene modification and targeting.

Innovation Solution

Development of novel linkers comprising 5 or more amino acids with specific residues, including proline and basic residues, that enhance the binding affinity and selectivity of zinc-finger modules for targets with specific gap lengths, allowing for more precise gene editing and modulation.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Reliability

If canonical linker sequences (e.g., TGEKP) are used to link zinc-finger modules, then the protein structure is maintained, but the binding affinity and selectivity for targets with base pair gaps is poor

Engineering Contradiction:
Improvebinding affinityVSAvoidselectivity for different gap lengths
Core Design Contradiction:
ReliabilityVSAdaptability or versatility

Solution Approach 1:

The patent applies local quality by designing linkers with specific local amino acid compositions (enriched in proline and basic residues like arginine and lysine) that are tailored to match specific gap lengths. Each linker has a distinct local sequence architecture optimized for binding to DNA targets with particular gap characteristics, enabling selective recognition of 0, 1, 2, or 3 base pair gaps between zinc-finger module subsites.

Inventive Principle:
Principle #3Local quality

Solution Approach 2:

The patent implements parameter changes by systematically varying linker length (5-17 amino acids) and composition (different ratios of proline to basic residues) to create a series of linkers with distinct binding properties. This allows the zinc-finger fusion proteins to discriminate between different gap lengths by changing the physical and chemical parameters of the linker region, thereby achieving both high affinity and selectivity.

Inventive Principle:
Principle #35Parameter changes

2Adaptability or versatility

If long flexible linkers are used to allow binding to targets with 1, 2, or 3 base pair gaps, then the adaptability increases, but the selectivity between different gap lengths is lost

Engineering Contradiction:
Improveability to bind targets with gapsVSAvoidgap length discrimination
Core Design Contradiction:
Adaptability or versatilityVSMeasurement precision

Solution Approach 1:

The patent resolves this contradiction by giving each linker a distinct local quality through specific amino acid sequences enriched in proline and basic residues. Rather than using uniform flexible linkers, the invention creates locally optimized linker regions with characteristic compositions that confer specificity for particular gap lengths, enabling the protein to distinguish between 0, 1, 2, or 3 base pair gaps while maintaining the ability to bind each type.

Inventive Principle:
Principle #3Local quality

3Ease of manufacture

If zinc-finger modules are linked with canonical linkers, then the design is simple, but the repertoire of targetable sites is limited

Engineering Contradiction:
Improvelinker design simplicityVSAvoidnumber of targetable sites
Core Design Contradiction:
Ease of manufactureVSAdaptability or versatility

Solution Approach 1:

The patent maintains ease of manufacture by providing a systematic framework for linker design based on controlled parameter changes. The invention establishes rules for varying linker length and composition (proline to basic residue ratios) to generate linkers with predictable binding specificities. This systematic approach expands the repertoire of targetable sites while keeping the design process relatively simple and methodical.

Inventive Principle:
Principle #35Parameter changes

Data Source

PatentEP3636766A1Compositions for linking zinc finger modules
Publication Date: 2020.04.15 SANGAMO THERAPEUTICS INC
  • EP3636766A1 patent drawingFigure 1A
  • EP3636766A1 patent drawingFigure 1B
  • EP3636766A1 patent drawingFigure 2A~2D

AI summary

Disclosed herein are compositions for linking DNA binding modules to allow for specific and selective binding to module subsites separated by 1 or more base pairs. Also described are methods of making and using compositions comprising these linkers.