J Domain Polypeptides Enhance Recombinant Protein Folding

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Solution Overview

Problem

Current methods for producing recombinant proteins face challenges in achieving proper folding, leading to inefficient expression and accumulation of improperly folded proteins, which can result in inactive aggregates and loss of functional protein, contributing to diseases such as prion-associated diseases, Alzheimer's, and cystic fibrosis.

Innovation Solution

Incorporation of protein expression enhancing polypeptides, specifically J domain analogs, into fusion proteins to enhance the expression and proper folding of target proteins by facilitating interaction with the Hsp70 chaperone machinery, thereby increasing the yield of properly conformed functional proteins.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Productivity

If recombinant protein expression is increased in host cells, then production quantity improves, but proper folding becomes more difficult leading to aggregation and loss of function

Engineering Contradiction:
Improveproduction quantityVSAvoidproper folding
Core Design Contradiction:
ProductivityVSReliability

Solution Approach 1:

The patent introduces J domain polypeptides as intermediary components that mediate between the Hsp70 chaperone system and client proteins requiring folding. These J domain polypeptides act as molecular mediators that stimulate ATP hydrolysis by Hsp70, thereby enhancing the chaperone's ability to facilitate proper folding of recombinant proteins at high expression levels, preventing aggregation while maintaining high productivity

Inventive Principle:
Principle #24Intermediary (Mediator)

2Reliability

If Hsp70 chaperone machinery is used to facilitate protein folding, then proper conformation is achieved, but the process requires multiple components including J proteins and NEFs increasing system complexity

Engineering Contradiction:
Improveproper conformationVSAvoidsystem complexity
Core Design Contradiction:
ReliabilityVSDevice complexity

Solution Approach 1:

The patent extracts and utilizes specifically the J domain polypeptide component from the complex Hsp70 chaperone machinery. By isolating and applying only the J domain portion, the invention simplifies the system while retaining the essential function of stimulating Hsp70 ATP hydrolysis to promote protein folding, thereby reducing complexity while maintaining effectiveness

Inventive Principle:
Principle #2Taking out (Extraction)

3Productivity

If improperly folded proteins accumulate, then functional protein yield decreases, but disease states such as prion-associated diseases, Alzheimer's, and cystic fibrosis may be contributed to

Engineering Contradiction:
Improvefunctional protein yieldVSAvoidmisfolding aggregates
Core Design Contradiction:
ProductivityVSObject-generated harmful factors

Solution Approach 1:

The patent converts the potentially harmful accumulation of misfolded proteins into a beneficial process by enhancing the Hsp70-J domain chaperone system. This converted system actively promotes proper folding of proteins that would otherwise misfold and aggregate, transforming a harmful situation into an opportunity to produce functional proteins while preventing disease-contributing aggregates

Inventive Principle:
Principle #22Blessing in disguise (Convert harm into benefit)

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

The use of J domain analogs in fusion proteins significantly increases the expression levels of target proteins, ensuring they are properly folded and functional, effectively addressing the challenges of protein misfolding and aggregation, and improving protein production yields.

Implementation Method 1

Binding by the J protein-client complex to Hsp70-ATP stimulates ATP hydrolysis, which causes a conformational change in the Hsp70 protein

Methodology Applied
Scientific EffectATP hydrolysis: Hydrolysis

Data Source

PatentEP2929045B1Protein expression enhancing polypeptides
Publication Date: 2020.12.02 SOLA BIOSCIENCES LLC
  • EP2929045B1 patent drawingFigure 1A~1C
  • EP2929045B1 patent drawingFigure 2A~2B
  • EP2929045B1 patent drawingFigure 3A~3B

AI summary

Fusion proteins comprising a protein expression enhancing polypeptide linked to a target protein binding domain and nucleic acid molecules encoding such fusion proteins are described for use in enhancing expression and/or location of a targeted protein of interest, for restoring lost functions in cells, and for treating disease. Additional fusion proteins comprising a target protein of interest modified with a fusion partner comprising a protein expression enhancing polypeptide are also disclosed.