Single-Cell RNA Translation Profiling with In Situ Ribosome Detection

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Solution Overview

Problem

Transcriptional profiles in single cells do not consistently correlate with proteomic profiles, indicating the need for improved methods to quantify protein production directly and accurately, as mRNA levels are an imperfect proxy for protein production and can be biased in defining cellular states.

Innovation Solution

A method for in situ ribosome profiling using proximity ligation with oligonucleotide probes and ribosome-specific antibodies to amplify and sequence actively translated mRNAs, providing precise spatial information on RNA translation status.

Engineering Contradictions & Design Principles

VSEngineering Contradiction Analysis

1Productivity

If mRNA levels are used as a proxy to estimate protein production, then the measurement process is simple and high-throughput, but the accuracy and reliability of protein production quantification deteriorates

Engineering Contradiction:
Improvethroughput of protein production quantificationVSAvoidaccuracy of protein production quantification
Core Design Contradiction:
ProductivityVSMeasurement precision

Solution Approach 1:

The patent introduces ribosomes as an intermediary marker to indirectly quantify protein production. Instead of directly measuring proteins (which is difficult) or using mRNA as a proxy (which is inaccurate), the method uses ribosomes bound to mRNA as a measurable intermediate that correlates with active translation and protein production, thereby resolving the accuracy-throughput contradiction

Inventive Principle:
Principle #24Intermediary (Mediator)

Solution Approach 2:

The patent replaces complex direct proteomic analysis methods with a nucleic acid-based approach. By using RNA-FISH and digital imaging to detect ribosome-bound mRNA, the method substitutes complex protein quantification with simpler, high-throughput optical detection while maintaining accuracy through ribosome-specific targeting

Inventive Principle:
Principle #28Mechanics substitution (Replace mechanical system)

2Measurement precision

If direct single-cell proteomic methods are developed, then the accuracy of protein production quantification improves, but the device complexity and difficulty of detection increase

Engineering Contradiction:
Improveaccuracy of protein production quantificationVSAvoidcomplexity of single-cell proteomic system
Core Design Contradiction:
Measurement precisionVSDevice complexity

Solution Approach 1:

The patent uses ribosomes as a convenient intermediary that is easier to detect than proteins themselves. Ribosomes can be targeted with specific antibodies or probes, providing a measurable signal that reflects protein production status without requiring direct protein detection, thus reducing system complexity while maintaining accuracy

Inventive Principle:
Principle #24Intermediary (Mediator)

Solution Approach 2:

The patent creates a detectable copy or proxy of the protein production state through ribosome-bound mRNA detection. By detecting the ribosome-mRNA complex rather than the protein itself, the method provides an accessible molecular copy that carries information about protein production without requiring direct protein measurement capabilities

Inventive Principle:
Principle #26Copying

3Adaptability or versatility

If spatial information of RNA translation is obtained through antibody staining, then the functional relevance of cellular data improves, but the measurement precision and signal detection difficulty increase

Engineering Contradiction:
Improvespatial information of RNA translationVSAvoidsignal detection difficulty
Core Design Contradiction:
Adaptability or versatilityVSDifficulty of detecting and measuring

Solution Approach 1:

The patent merges multiple detection approaches by combining ribosome-specific antibodies with fluorescently conjugated probes in a single assay. This combination allows simultaneous detection of translation status and spatial location, integrating functional information with positional data while using the fluorescent signal to enhance detectability

Inventive Principle:
Principle #5Merging (Combining)

Solution Approach 2:

The patent employs fluorescent labeling of ribosome-bound mRNA complexes, utilizing color/fluorescence changes as a detectable signal. The fluorescent conjugate on the antibody or probe provides a strong, easily detectable signal that indicates the presence and location of actively translating mRNA, thereby reducing detection difficulty while maintaining spatial precision

Inventive Principle:
Principle #32Color changes

Applied Scientific Principles

This section explains which scientific principles are used to turn an abstract innovation direction into a practical engineering solution.

Function Achieved in This Case

Enables high-throughput characterization of RNA translation status, bridging the gap between transcriptome and proteome, and facilitating disease diagnosis, treatment, and drug discovery by accurately quantifying protein production in single cells.

Implementation Method 1

a second probe comprises a portion that recognizes the ribosome and an oligonucleotide portion that is complementary to a portion of the first probe

Methodology Applied
Scientific EffectComplementary base pairing:

Implementation Method 2

performing rolling circle amplification to amplify the circular oligonucleotide using the second probe as a primer to produce one or more concatenated amplicons

Methodology Applied
Scientific EffectRolling circle amplification:

Implementation Method 3

ligating the 5' end and the 3' end of the first probe together to produce a circular oligonucleotide

Methodology Applied
Scientific EffectProximity ligation:

Data Source

PatentEP4363614B1Single-cell profiling of RNA translation status
Publication Date: 2025.08.06 THE BROAD INST INC
  • EP4363614B1 patent drawingFigure 1
  • EP4363614B1 patent drawingFigure 2A~2B
  • EP4363614B1 patent drawingFigure 2C~2D

AI summary

The present disclosure provides methods and systems for profiling RNAs being translated in a cell. Also provided by the present disclosure are methods for diagnosing a disease or disorder in a subject based on a profile of the RNAs being translated in a cell, including cells within an intact tissue. Methods of screening for or testing a candidate agent capable of modulating translation of one or more RNAs are also provided by the present disclosure. The present disclosure also provides methods for treating a disease or disorder in a subject in need thereof. Pairs of probes and sets of probes comprising oligonucleotide portions, which may be useful for performing the methods described herein, are also described by the present disclosure. Additionally, the present disclosure provides kits comprising any of the probes described herein.