PRODUCTS AND METHODS FOR TREATING AMYOTROPHIC MULTIPLE SCLEROSIS
CY1125950T1Undetermined Publication Date: 2026-04-17RES INST AT NATIONWIDE CHILDRENS HOSPITAL
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Patent Information
- Application Number
- CY20231100162T
- Authority / Receiving Office
- CY · CY
- Patent Type
- Patents
- Current Assignee / Owner
- Priority Date
- 2013-08-27
- Filing Date
- 2023-03-24
- Publication Date
- 2026-04-17
- Estimated Expiration
- 2043-03-24
Abstract
The present invention relates to RNA-based methods for inhibiting the expression of the superoxide dismutase 1 (SOD-1) gene. Recombinant adeno-associated viruses of the invention deliver DNAs encoding RNAs that neutralize the expression of SOD-1. The methods have application in the treatment of amyotrophic lateral sclerosis.
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