Modified aav capsids and uses thereof

CN114787179BActive Publication Date: 2026-06-23SOLID BIOSCIENCES INC
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Patent Information

Authority / Receiving Office
CN · China
Patent Type
Patents(China)
Current Assignee / Owner
SOLID BIOSCIENCES INC
Filing Date
2020-10-09
Publication Date
2026-06-23

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Abstract

The methods described herein provide a modified VP1 capsid capable of preferentially targeting a gene of interest (GOI) within muscle tissue and a recombinant adeno-associated virus (rAAV) having a GOI encapsidated with the modified VP1 capsid and uses thereof.
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Citation Information

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