COMPOUNDS AND METHODS FOR FORMULATING SMN2
CY1125819T1Undetermined Publication Date: 2026-04-17IONIS PHARMACEUTICALS INC
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Patent Information
- Application Number
- CY20221100781T
- Authority / Receiving Office
- CY · CY
- Patent Type
- Patents
- Current Assignee / Owner
- Priority Date
- 2016-07-15
- Filing Date
- 2022-12-12
- Publication Date
- 2026-04-17
- Estimated Expiration
- 2042-12-12
Abstract
Disclosed herein are compounds, compositions and methods for modulating the splicing of SMN2. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for the treatment of spinal muscular atrophy.
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