A mutant col4a5 gene and its application
A gene and gene numbering technology, applied to the mutated COL4A5 gene and its application field, can solve the problems of high time consumption and cost, and achieve the effect of significant genetic heterogeneity
Patent Information
- Authority / Receiving Office
- CN · China
- Patent Type
- Patents(China)
- Current Assignee / Owner
- Publication Date
- 2019-08-13
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Abstract
Description
technical field
[0001] The invention belongs to the field of biomedicine and relates to a mutated COL4A5 gene and its application. Background technique
[0002] Alport syndrome (alport syndrome, AS) is a hereditary kidney disease characterized by progressive renal function decline and glomerular basement membrane structural abnormalities with neurological deafness and eye disease. At present, there are three ways of inheritance of AS: X-linked dominant inheritance (XL; about 80%), autosomal recessive inheritance (AR; about 15%) and autosomal dominant inheritance (AD; very few), respectively. It is caused by mutations in the genes COL4A5 (or COL4A5 and COL4A6), COL4A3 and (or) COL4A4 encoding different α chains of type IV collagen.
[0003] X-linked genetic disease-causing genes include COL4A5 (or COL4A5 and COL4A6). COL4A5 is located at Xq22 and is the gene most closely associated with AS. Since the first COL4A5 mutation was discovered, more than 400 gene mutations have bee...
Examples
Embodiment Construction
[0038] experimental method:
[0039] 1. Establishment of AS genetic resource bank.
[0040] 1.1 Collect the clinical data and blood samples of the following three types of AS patients:
[0041] 1.1.1 Three or more generations of AS families with X-chromosome-linked dominant inheritance.
[0042] 1.1.2 Collect small families with X-linked dominant inheritance.
[0043] 1.1.3 Collect sporadic cases with negative staining of type IV collagen α5 chain without family history.
[0044] 1.2 Genomic DNA extraction:
[0045] Using TIANamp Blood DNA Extraction Kit (Tiangen Biotech Co. Ltd, Beijing, China), the patient's genomic DNA was extracted from the collected patient's peripheral blood according to the protocol provided by the manufacturer.
[0046] 2. Discover new mutations in the known pathogenic gene COL4A5 of AS.
[0047] 2.1 Design and customize AS-related gene capture chip:
[0048] 2.1.1 Selection of candidate genes:
[0049] The gene trap chip covers four AS-causing ...